首页|Gene therapy for spinal muscular atrophy:perspectives on the possibility of optimizing SMN1 delivery to correct all neurological and systemic perturbations
Gene therapy for spinal muscular atrophy:perspectives on the possibility of optimizing SMN1 delivery to correct all neurological and systemic perturbations
School of Pharmacy and Bioengineering,Keele University,Keele,UK
Wolfson Center for Inherited Neuromuscular Disease,TORCH Building,RJAH Orthopaedic Hospital,Oswestry,UK
AGCTIab.org,Center of Gene and Cell Therapy,Department of Biological Sciences,School of Life Sciences and the Environment,Royal Holloway University of London,Egham,UK