中国新药杂志2024,Vol.33Issue(24) :2546-2549.

重症肌无力治疗药物zilucoplan

Myasthenia gravis treatment drug:zilucoplan

刘爽 刘畅 江丹沁 苏畅 唐一楠
中国新药杂志2024,Vol.33Issue(24) :2546-2549.

重症肌无力治疗药物zilucoplan

Myasthenia gravis treatment drug:zilucoplan

刘爽 1刘畅 1江丹沁 1苏畅 1唐一楠1
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作者信息

  • 1. 中日友好医院药学部,北京100029
  • 折叠

摘要

重症肌无力是一种由抗体介导的免疫性疾病,常表现为骨骼肌无力及易疲劳性,通常使用传统治疗药物即可取得较好疗效,然而仍有部分患者症状并未得到良好改善,因此新药研发至关重要.zilucoplan注射液(商品名:Zilbrysq)为补体抑制剂,是治疗重症肌无力的新药,美国FDA于2023年10月17日批准zilucoplan注射液上市.本文对zilucoplan的药理作用、作用机制、药动学及用法用量等简要介绍,旨在为临床用药提供参考.

Abstract

Myasthenia gravis is an immune disease mediated by antibodies,often manifested as skeletal muscle weakness and fatigue,treatment using traditional drugs usually can achieve good results,but there are still some patients whose symptoms have not been well improved,so the development of new drugs is very important.And zilucoplan injection ( trade name:Zilbrysq ) is a complement inhibitor,a new drug for the treatment of myasthenia gravis.The US FDA approved zilucoplan injection on October 17,2023.The pharmacological action,mechanism of action,pharmacokinetics,and usage and dosage of zilucoplan were briefly introduced in this paper,aiming to provide reference for its clinical use.

关键词

zilucoplan/重症肌无力/补体抑制剂/药理学/疲劳

Key words

zilucoplan/myasthenia gravis/complement inhibitor/pharmacology/fatigue

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出版年

2024
中国新药杂志
中国医药科技出版社 中国医药集团总公司 中国药学会

中国新药杂志

CSTPCD北大核心
影响因子:1.039
ISSN:1003-3734
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